Stay Curious

SIGN UP FOR OUR WEEKLY NEWSLETTER AND UNLOCK ONE MORE ARTICLE FOR FREE.

Sign Up

VIEW OUR Privacy Policy


Discover Magazine Logo

WANT MORE? KEEP READING FOR AS LOW AS $1.99!

Subscribe

ALREADY A SUBSCRIBER?

FIND MY SUBSCRIPTION
Advertisement

A Ten-Year Check-Up Shows Gene Therapy Patients are Alive and Well

Discover the success of gene therapy for SCID, offering hope with long-term cures for severe combined immunodeficiency. Click to learn more!

Newsletter

Sign up for our email newsletter for the latest science news

Sign Up

What's the News: Medicine in the age of genes overflows with daring new techniques and treatments, from personalized chemotherapy to prenatal genetic testing, each heralded as a game-changer. But rarely do we get an assessment of a treatment's long-term good, which is why recent papers following up on one of the most controversial genetic treatments, gene therapy, are making waves: though one patient developed leukemia from the treatment, 13 of 16 kids treated with gene therapy for a severe immune disorder at least 9 years ago have been cured, adding to the sense that the field is on its way to recovery from early setbacks. The Backstory:

Gene therapy involves correcting errors in cells' genetic code. In the case of some of these children, who had no functioning immune system due to X-linked SCID---severe combined immunodeficiency, or "bubble boy" syndrome---bone marrow transplants had been the only way to effectively treat ...

Stay Curious

JoinOur List

Sign up for our weekly science updates

View our Privacy Policy

SubscribeTo The Magazine

Save up to 40% off the cover price when you subscribe to Discover magazine.

Subscribe
Advertisement

0 Free Articles